First Two Children Receive New Gene Therapy for Rett Syndrome
Neurogene Inc.
Phase 1/2 trial showed the safety and therapeutic potential of administering a novel transgene
Phase 1/2 trial showed the safety and therapeutic potential of administering a novel transgene
Per the WHO records, more than 39 million people were living with HIV at the end of 2022
Researchers are finding clues that may help treat rare and deadly diseases using mini-organs and advanced technology