Structure and Function of Newly Discovered CRISPR Immune System
Utah State University
In tandem papers in Nature, researchers report effects of Cas12a2
Gene Editing
Study Links Molecular Changes to Long COVID a Year after Hospitalization
Mount Sinai School of Medicine
Study is one of the first to associate long COVID symptoms with changes in gene expression during acute COVID-19
Gene Mutation Leading to Autism Found to Overstimulate Brain Cells
Rutgers University
Rutgers-led study highlights potential of new techniques to study mental disorders
Removing Roadblocks in Cell and Gene Therapy Quality Control
Marwan Alsarraj, MS
Droplet digital PCR (ddPCR) technology provides unmatched quality control for cell and gene therapies
New CRISPR-Cas Approach Permits More Precise DNA Cleavage
Massachusetts General Hospital
So-called SpRYgests enable DNA cutting at practically any sequence for DNA editing
Discovery Broadens Scope of Use of CRISPR Gene Editing
Northwestern University
Combining two powerful therapeutic technologies may change the landscape of medical therapeutics
Researchers Discover Dozens of Genetic Defects Important for Immune Defense
University of Helsinki
Results suggest that targeted inhibition of certain NFKB signaling pathway components is an viable therapeutic approach
How CRISPR-Cas9 Contributed to Rare Disease Research in 2021
Brydie Thomas-Moore, PhD
Research from this past year highlights the potential of CRISPR-Cas9 technology in modeling and treating rare disease
Exploring Alternatives to CRISPR Gene Editing Techniques
Marwan Alsarraj, MS
Transposons have the potential to make DNA editing easier, cheaper, and safer
Gene Therapy Restores Immune Function
Miriam Bergeret, MSc
Researchers have successfully treated a rare genetic immunodeficiency disorder using an investigational gene therapy